People
PHD STUDENTS
Daniel Bauersachs
PhD student
Post mitotic neuron gene repair, base editing gene therapy technology development and delivery for IRF2BPL and SYNGAP1 related disorders.
Sandhya Mani
PhD student
Sequence replacement gene therapy technology development and delivery in vitro and in vivo using engineered Virus Like Particles (eVLPs) for Huntington’s diease and IRF2BPL spectrum of diseases.
Louise Bomholtz
PhD student
Post mitotic neuron gene repair and delivery using base editors, and engineered Virus Like Particles (eVLPs) for SYNGAP1 and IRF2BPL related disorders
Sara del Rey
PhD student
Stem cell based IRF2BPL disease modeling, 3D brain organoids, high content phenotyping, drug screening.
SCIENTISTS
Niels Weissbach
Homology independent sequence replacement based gene therapy development for IRF2BPL/NEDAMSS and Huntington’s Disease (postdoctoral researcher)
Post Doctoral Researcher
Somatic cell genome editing technology development – recruitment phase.
Technical Assistance
Stephanie Petzold
Gene editing, stem cells, molecular cloning.
Mandy Gerlach
Stem cells.
Anja Vanessa Kirsch
Stem cells, molecular cloning, stem cell clonal isolation
enJoy
Blue Heeler
RotaTION and visiting
Krishna Nilesh Patel
iDream for a Cure fellowship 2025
AAVs, VLPs development (Student visitor, TX, USA)
Sofia Notopoulou
Position: Bayer Fellowship 2026
Gene augmentation and delivery in treatment of Parkinson’s diease (PD)
Ludovica Rigat
Charité – Universitätsmedizin Berlin
The role of microglia in neurodegeneration, integration of microglia into 3D brain organoids.
JOINT RESEARCH COLLABORATIVE INSTITUTIONS (under collaboration research agreements, CRAs)
University of California San Diego (UCSD)
9500 Gilman Drive, La Jolla, CA 92093-0910, United States, CRA no OIC_SD2020-065
Center for Gene Therapy, Research Institute at Nationwide Children’s Hospital
700 Children’s Drive, Columbus, Ohio 43205, United States/Next Gen Precision Health, Missouri, United States, CRA no NCH 2020-0002 (00271258 4)
Genetics, Sanford Research
2301 East 60th Street North, Sioux Falls, South Dakota 57104, United States
Sanford Contract no 2168
Department of Neurology, Mayo Clinic Jacksonville
4500 San Pablo Road, Jacksonville 32224, United States, CRA ID: 558D6709-B382-4AB9-ACB9-22ACECEA8642
Nemours Children's Hospital
1600 Rockland Rd., Wilmington, DE, United States
CRA CASE NO. NEMOURS FOUNDATION: Nemours Children’s Hospital, Delaware
The UNIVERSITY MEDICAL CENTER UTRECHT (UMCU)
Heidelberglaan 100, 3584, CX Utrecht, the Netherlands, CRA V1, November 25th 2021
COLLABORATIVE SERVICE FACILITIES
Core Facility Induced Pluripotent Stem Cells Helmholtz Center Munich
Ingolstädter Landstraße 1 85764 Neuherberg, Building 35.34, Room 217